Obeticholic acid

Pronunciation: oh-BET-i-KOL-ik AS-id.

Generic name
obeticholic acid
Brand names
OCALIVA
Drug class
Farnesoid X receptor agonist; bile-acid derivative
Form
Tablet in countries where an authorised product remains available
Route
Oral
Legal status
Regulatory status differs by country; withdrawn in the United States, revoked in the European Union, and actively registered in Australia as of 22 July 2026

Supply Rules Vary

Trade names by country: United States · Canada · Australia

Australia: OCALIVA (4) · Full directory

What obeticholic acid is and how it works

Obeticholic acid is a farnesoid X receptor agonist that was developed for primary biliary cholangitis (PBC). It was formerly authorised in the United States and European Union under the brand Ocaliva, but those authorisations are no longer current. Australia retains an active registered product at the audit date. (1) (3) (5) (4)

Regulators reached different current outcomes, so this page cannot give a global statement that the medicine is approved, available, beneficial, or suitable. Existing patients require individual hepatology review of liver status, local authorisation, access, benefit, risks, and alternatives.

Mechanism of action: how obeticholic acid works

Obeticholic acid is a farnesoid X receptor agonist. Mechanism alone does not establish clinical benefit or current authorisation. (2) (3)

What obeticholic acid is used for

Former United States indication

Ocaliva formerly had accelerated approval for PBC with ursodeoxycholic acid in adults with an inadequate response, or alone in adults unable to tolerate ursodeoxycholic acid. That indication was withdrawn on 24 November 2025 and must not be presented as current US use. (1)

European Union status

The EU conditional marketing authorisation was revoked after confirmatory evidence failed to establish clinical benefit and regulators concluded that benefits no longer outweighed risks. New patients should not be started outside a clinical trial; exceptional existing-patient access may depend on national named-patient or compassionate-use arrangements. (3)

Australian registered indication

Australian regulator records support use for PBC with ursodeoxycholic acid in adults with inadequate response or alone in adults unable to tolerate ursodeoxycholic acid. This is Australian status only and still requires the current Product Information and specialist assessment. (5) (4)

Before taking obeticholic acid

Do not take / not appropriate for

  • Do not start or obtain obeticholic acid in a country where it is withdrawn, revoked, unapproved, or unavailable through a lawful specialist pathway. (country-specific) (1) (3)
  • Do not use historical US or EU dosing information as current treatment guidance. (all public users) (1) (3)

Tell your clinician about

  • Your country and how the medicine was supplied.
  • Cirrhosis, portal hypertension, liver decompensation, ascites, variceal bleeding, encephalopathy, jaundice, or a liver transplant assessment.
  • New or worsening itching, dark urine, pale stools, swelling, confusion, bleeding, infection, or abdominal distension.
  • Every medicine, bile-acid binder, supplement, alcohol use, pregnancy, or breastfeeding.
  • Any interruption, dose change, access problem, or advice received after a regulatory withdrawal or revocation.
(2) (3)

How to take obeticholic acid

  • This page does not provide a dose or schedule because current authorisation differs by country and historical labels are unsafe substitutes for current local Product Information.
  • Existing patients should contact their hepatology team promptly and continue only according to that team's current lawful plan.
  • Do not restart after an interruption, alter a dose for itching, or combine it with bile-acid medicines without specialist instructions.
  • Do not purchase Ocaliva online or import it based on information from another country.
(1) (3) (4)

Procedures and treatment changes

Tell the treating team before surgery, procedures, or any medicine change. Do not alter treatment without the responsible clinician. (1) (2) (3) (4) (5)

Missed dose

Do not use an old leaflet or online schedule. Contact the hepatology or dispensing team for country- and product-current instructions, particularly after any treatment interruption or regulatory access change.

Overdose

Seek urgent poison-information and medical advice for a possible overdose. Because serious liver injury is a central risk, provide the product, amount, timing, liver history, and current symptoms. Do not wait for jaundice or confusion. (2)

Side effects

Historical and current-country product information identifies important liver and pruritus risks. The current local label and hepatology team must control individual counselling.

Pruritus (itching)

What to notice: New, worsening, persistent, or sleep-disrupting itching or skin injury from scratching.

What to do: Contact the hepatology team. Do not alter or skip doses using a historical regimen. (2)

Possible worsening liver function

What to notice: New fatigue, nausea, poor appetite, dark urine, pale stools, worsening itch, jaundice, swelling, or abdominal enlargement.

What to do: Obtain urgent hepatology assessment; emergency care is needed for confusion, bleeding, collapse, or severe illness. (2)

Serious warnings

Serious liver injury or hepatic decompensation — emergency

Symptoms: Jaundice, confusion or drowsiness, vomiting blood, black stools, marked abdominal swelling, severe weakness, collapse, or rapidly worsening illness.

Action: Seek emergency medical care and tell the team about obeticholic acid and the underlying liver disease. (2)

Use after withdrawal or revocation — urgent_regulatory

Symptoms: A new prescription, online offer, cross-border supply, or old stock in the United States or European Union after the applicable authorisation ended.

Action: Do not start or purchase it. Contact the national regulator, pharmacist, and hepatology team to verify lawful status and alternatives. (1) (3)

Interactions

Medicine or testEffectAction
Bile-acid binding resins and other PBC treatmentTiming and co-treatment can affect exposure or treatment planning, but historical label instructions must not be generalised after withdrawal or revocation.The hepatology pharmacist must review the exact current local product information and complete medicine list. (4)
Medicines affected by liver function or with narrow therapeutic rangesProgressive liver disease and product-specific interactions can alter safety and monitoring needs.Obtain specialist medication reconciliation and liver-function review; do not use an automated interaction result as clearance. (2)

Pregnancy, breastfeeding, kidney/liver function, age

Cirrhosis or portal hypertension

This is a high-risk context for serious liver harm. Historical warnings and current local labeling require specialist staging and may prohibit treatment. A general page cannot determine eligibility. (2)

Pregnancy and breastfeeding

Current country-specific evidence and treatment necessity require hepatology and obstetric review. Do not rely on a withdrawn or revoked label. (4)

Existing patients in withdrawn or revoked markets

Contact the treating specialist promptly to discuss status, benefit, risk, monitoring, lawful access if exceptional pathways exist, and alternatives. Do not stop abruptly without clinical advice unless emergency care directs you. (3) (1)

Monitoring

Before starting

  • Do not initiate from this page. Verify current national authorisation and lawful supply.
  • Confirm PBC diagnosis, prior ursodeoxycholic-acid response or intolerance, cirrhosis stage, portal-hypertension or decompensation history, liver tests, symptoms, interactions, and alternatives using current local guidance.

During treatment

  • Use the current local Product Information and hepatology plan for liver biochemistry, symptoms, decompensation signs, pruritus, lipids, adherence, and ongoing benefit-risk review.
  • Recheck regulatory status and access when treatment crosses borders or a regulator issues a new decision.
(2) (3) (4)

Storage

Do not retain, share, import, or use old or cross-border stock without pharmacist and specialist verification of the exact product, expiry, storage history, and current lawful status.

Professional regulatory and clinical context

Do not prescribe from this summary. Verify the live national register, current Product Information, hepatology guideline, patient access pathway, and local withdrawal/revocation communications.

United States and European Union

Indication: PBC

Dose summary: No current authorised regimen is displayed because the US indication was withdrawn and the EU marketing authorisation revoked.

Renal context: Not applicable as prescribing guidance; manage existing-patient transition through current national and specialist pathways. (1) (3)

Australia

Indication: Country-defined PBC indication

Dose summary: Active registration is verified, but dosing is intentionally omitted until the current Australian Product Information is independently extracted, versioned, and clinically reviewed.

Renal context: Use current Australian Product Information and individual hepatic status; no web-derived adjustment. (4) (5)

Mechanism of action

Hepatic guidance

Advanced liver disease, portal hypertension, decompensation, and changing liver status are central safety determinants requiring specialist management.

Overdose note

Provide urgent toxicology and hepatology assessment with liver-focused monitoring and supportive care. (2) (3)

Frequently asked questions

Is Ocaliva still approved?

It depends on the country. The US indication was withdrawn in November 2025 and the EU authorisation was revoked. Australia still showed active registration on 22 July 2026. Always verify the current national register. (1) (3) (4)

Should I stop Ocaliva if I currently take it?

Contact your hepatology team promptly. Do not stop or change it solely from a web page unless an emergency clinician directs you; your local status, liver condition, benefit, risk, access pathway, and alternatives must be reviewed. (3)

Can I buy Ocaliva from another country?

Do not use online or cross-border supply. Authorisation, legal import, product authenticity, monitoring, and safety differ, and the medicine is withdrawn or revoked in major markets. (1) (3)

What is the mechanism of action of obeticholic acid?

Obeticholic acid is a farnesoid X receptor agonist. Mechanism alone does not establish clinical benefit or current authorisation. (2) (3)

What is the generic name of Obeticholic acid?

The generic name is obeticholic acid. It is sold under brand names including OCALIVA. (1) (3) (4)

What class of drug is obeticholic acid?

Obeticholic acid is classed as: Farnesoid X receptor agonist; bile-acid derivative. (1) (3) (4)

References

  1. Withdrawn non-malignant accelerated approvals — OcalivaU.S. Food and Drug Administration · United States · dated 2025-11-24 · accessed 2026-07-22 · source 1
  2. FDA drug safety communications — Ocaliva serious liver injuryU.S. Food and Drug Administration · United States · dated 2024-12-12 · accessed 2026-07-22 · source 2
  3. Ocaliva Article 20 referral — revocation of conditional marketing authorisationEuropean Medicines Agency · European Union · dated 2025-01-07 · accessed 2026-07-22 · source 3
  4. OCALIVA obeticholic acid 10 mg tablet bottle — ARTG 293378Therapeutic Goods Administration · Australia · accessed 2026-07-22 · source 4
  5. OCALIVA prescription medicine registrationTherapeutic Goods Administration · Australia · dated 2018-07-18 · accessed 2026-07-22 · source 5

Brand names by country

Single-ingredient obeticholic acid names are shown separately by country. Product availability, strengths, and supply rules can change; combination products are not included here.

Priority countries

United States

  • Ocaliva (1)indication withdrawn 2025-11-24 · Not represented as currently authorised

Canada

  • OCALIVA

Australia

  • OCALIVA (4)active register product · 10 mg · Amdipharm Mercury Australia Pty Ltd
View brands in additional countries.

European Union

Ocaliva (3)

This page records country-specific regulatory and safety information. It is not a prescription, dose, recommendation to start or stop treatment, access advice, or substitute for a hepatology team and current national regulator information.

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